Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle

V. Arechavala-Gomeza, I.R. Graham, L.J. Popplewell, Abbie Adams, A. Aartsma-Rus, M. Kinali, J.E. Morgan, J.C. Van Deutekom, Steve Wilton, G. Dickson, F. Muntoni

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