Original language | English |
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Pages (from-to) | 1625-1638 |
Journal | Human Molecular Genetics |
Volume | 21 |
Issue number | 7 |
DOIs | |
Publication status | Published - 2012 |
A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse
P.N. Porensky, Chalermchai Mitrpant, V.L. Mcgovern, A.K. Bevan, K.D. Foust, B.K. Kaspar, Steve Wilton, A.H. Burghes
Research output: Contribution to journal › Article › peer-review
208
Citations
(Scopus)