Evaluating an allele-specific genetic therapy for congenital myopathy caused by dominant mutations in the skeletal muscle actin (ACTA1) gene

Project Details

StatusFinished
Effective start/end date30/05/1830/11/19

Funding

  • Association Francaise contre les Myopathies (AFM): AUD29,020.00
  • Association Francaise contre les Myopathies (AFM): AUD42,070.00